Gene Therapy Advancements Surge, Leading to the Return of the 7th Gene Therapy for Rare Disorders Summit

The gene therapy landscape has witnessed an unprecedented surge in advancements, with more therapies gaining FDA approval in the past year than in the previous five years combined.

To address the evolving landscape and maximize the potential of late-stage gene therapy assets, the highly anticipated 7th Gene Therapy for Rare Disorders Summit is set to return. This summit aims to confront the significant clinical, manufacturing, regulatory, and commercial challenges currently confronting gene therapy programs.

Scheduled to take place, 26-29 March, Boston, the summit will bring together industry leaders, regulatory bodies, patient non-profits, payers, and key service providers. This gathering serves as the premier forum for collectively advancing rare gene therapy programs into and through clinical stages.

“I am looking forward to multistakeholder engagement including with developers, regulators, patient community and others at the 2024 GTx RD Summit to together propel the gene therapy field forward to help address unmet needs for rare disease patients.” Says Nimi Chhina, Executive Director, Head of Global Research and Development & Regulatory Policy, BioMarin.

This summit provides a unique opportunity to stay informed, form connections with top decision-makers, and address specific clinical, manufacturing, regulatory, and commercial challenges.

As the gene therapy landscape continues to evolve, marked by a growing wave of approvals and programs entering clinical development, the Gene Therapy for Rare Disorders Summit returns as the industry’s leading platform for benchmarking success stories and addressing key challenges.

The summit’s program, co-created by a faculty of senior decision-makers, promises to be a one-stop shop for rare gene therapy expertise. Attendees can expect cutting-edge talks, multistakeholder panel discussions, and expert-led group discussions, providing strategic insights to overcome challenges and minimize setbacks in late-stage programs.

Don’t miss this opportunity to stay ahead of the curve in the gene therapy field. Register now to secure your place at the 7th Gene Therapy for Rare Disorders Summit and ensure the success of your gene therapy initiatives.