Diseases

Rare cancers inherently make it difficult to collect data, build clinical expertise and treat affected patients – challenges which are best addressed through collaboration in…
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Mission Therapeutics and AbbVie announced a collaboration in the research and preclinical development of specified DUB inhibitors for the treatment of Alzheimer’s Disease and…
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Amgen and Provention Bio announced a licensing and co-development agreement for AMG 714, identified by Provention as PRV-015. AMG 714 is a novel anti-IL-15 monoclonal antibody being…
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Vertex Pharmaceuticals (Europe) Limited announces that the European Medicines Agency’s (EMA) Committee for Medicinal Products for Human Use (CHMP) adopted a positive opinion for…
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The first clinical trial of a completely novel and unprecedented approach to modifying the progression of Alzheimer's disease has opened in London. The study is being conducted in the…
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Wave Life Sciences Ltd. announced plans to design and advance stereopure oligonucleotide therapeutics for the potential treatment of rare, inherited eye diseases. Wave’s research in…
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Evotec AG announced that CHDI Foundation, Inc. has extended its collaboration with Evotec through to 2023. Over this period, CHDI may fund up to 75 full-time scientists at Evotec.…
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Regen BioPharma has identified a series of small molecule drugs that inhibit NR2F6. Regen's screening process demonstrated that its recently identified novel chemical compounds appear…
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Evotec AG announced that CENTOGENE AG and Evotec entered into a global strategic collaboration agreement for joint drug discovery projects, developing compounds to treat rare genetic…
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Roche announced that the China National Drug Administration (CNDA) has granted marketing authorisation for Alecensa (alectinib) as a monotherapy treatment for patients with anaplastic…
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AstraZeneca announced that the Japanese Ministry of Health, Labour and Welfare (MHLW) has approved Tagrisso(osimertinib) for the 1st-line treatment of patients with inoperable or…
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Sun Pharmaceutical Industries Ltd. announced that Sun Pharma has received approval for CEQUA (cyclosporine ophthalmic solution) 0.09%, from the U.S. Food and Drug Administration (FDA).…
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Researchers funded by the National Eye Institute (NEI) have reversed congenital blindness in mice by changing supportive cells in the retina called Müller glia into rod photoreceptors.…
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The U.S. Food and Drug Administration issued new scientific recommendations aimed at encouraging more widespread innovation and development of novel medication-assisted treatment (MAT)…
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Ambys Medicines and Takeda Pharmaceutical Company Limited announced that they have entered into a partnership to support the advancement of the Ambys platform and pipeline. “We are…
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Glenmark Pharmaceuticals S.A. and Harbour BioMed announced that they have entered into an exclusive license agreement for the Greater China territory to develop, manufacture and…
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PTC Therapeutics and Akcea Therapeutic an affiliate of Ionis Pharmaceuticals announced a collaboration under which PTC will commercialize two of Akcea's rare disease drugs in Latin…
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Roche announced that the European Medicines Agency (EMA) has granted PRIME (PRIority MEdicines) designation for the company’s investigational medicine RG6042 (formerly known as…
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BioNTech AG and Genevant Sciences announced that they have entered into a collaboration to develop five mRNA therapeutic programs for rare diseases with high unmet medical need. The…
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Treating advanced breast cancer with three drugs instead of one could boost the effectiveness of treatment and stop tumours developing resistance, a new study reports. Researchers…
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